Unlocking CNS Delivery: A Lipid Nanoparticle Platform Inspired by Natural Brain Chemistry
Time: 3:15 pm
day: Conference Day One
Details:
- Developing unique lipid nanoparticles optimized for CNS applications to enable precise delivery of genetic medicines (such as RNA therapeutics and CRISPR gene editing) for neurodegenerative diseases
- Showcasing in vitro gene editing data and in vivo biodistribution insights to highlight targeted delivery to specific brain regions and cell types
- Huntington’s Disease and MSH3 as clinical targets for translational application of the platform
