Rebecca Haley

Company: Script Biosciences

Job title: Senior Scientist

Seminars:

Unlocking CNS Delivery: A Lipid Nanoparticle Platform Inspired by Natural Brain Chemistry 3:15 pm

Developing unique lipid nanoparticles optimized for CNS applications to enable precise delivery of genetic medicines (such as RNA therapeutics and CRISPR gene editing) for neurodegenerative diseases Showcasing in vitro gene editing data and in vivo biodistribution insights to highlight targeted delivery to specific brain regions and cell types Huntington’s Disease and MSH3 as clinical targets…Read more

day: Conference Day One

ROUNDTABLE DISCUSSION: Tailoring Your Delivery System to Different Gene-Editing Payloads Including CRISPR/CAS & Beyond 3:45 pm

How do different gene-editing payloads, including CRISPR/Cas9, base editing v prime editing, impact delivery system design and optimization? At what point do improvements in gene-editing technology outweigh the feasibility of adapting delivery systems—when is ‘good enough’ truly enough? What are the biggest challenges in adapting delivery technologies for next-generation gene editors, and how can lessons…Read more

day: Conference Day One